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20 May 2022

PTC Therapeutics Receives Positive CHMP Opinion for Upstaza™ for the Treatment of AADC Deficiency

Author: admintech | Filed under: Press Release

– First ever gene therapy directly administered into the brain – – Recommended for regulatory approval by EMA – – Results demonstrated sustained improvements in motor and cognitive function – – Conference call scheduled for Monday, May 23, at 8 a.m. ET – SOUTH PLAINFIELD, N.J., May 20,…